RARE - Ultragenyx Pharmaceutical Inc.
Price:
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--
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CONSENSUS:
Buy
DETAILS
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PRICE TARGET:
$48.36
DETAILS
HIGH:
$67.00
LOW:
$26.00
MEDIAN:
$45.00
CONSENSUS:
$48.36
UPSIDE:
106.76%
| Metric | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 | 2018 | 2017 | 2016 | 2015 | 2014 | 2013 | 2012 | 2011 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Revenue | |||||||||||||||
| Revenue | 673 | 560.2 | 434.2 | 363.3 | 351.4 | 271.0 | 103.7 | 51.5 | 2.6 | 0.1 | 0 | 0 | 0 | 0 | 0 |
| Cost of Revenue | 109 | 76.7 | 45.2 | 28.3 | 16.0 | 6.1 | 9.0 | 1.1 | 0.0 | 183.2 | 1.4 | 0 | 0 | 0 | 0 |
| Gross Profit | 564 | 483.5 | 389.0 | 335.0 | 335.4 | 264.9 | 94.7 | 50.3 | 2.6 | (183.1) | (1.4) | 0 | 0 | 0 | 0 |
| Operating Expenses | |||||||||||||||
| R&D Expenses | 750 | 697.9 | 648.4 | 705.8 | 497.2 | 412.1 | 357.4 | 294.0 | 231.6 | 183.2 | 114.7 | 46.0 | 27.8 | 12.6 | 4.7 |
| SG&A Expenses | 349 | 321.6 | 309.8 | 278.1 | 220.0 | 182.9 | 161.5 | 127.7 | 99.9 | 64.9 | 33.0 | 10.8 | 4.5 | 3.3 | 1.8 |
| Other Expenses | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 4.0 | 0 | 2.2 | (0.2) | 0 | 0 | 0 | (0.0) |
| Operating Expenses | 1,099 | 1,019.5 | 958.2 | 983.9 | 717.1 | 595.0 | 518.9 | 421.7 | 331.6 | 248.1 | 147.7 | 56.8 | 32.3 | 16.0 | 6.6 |
| Operating Income | |||||||||||||||
| Operating Income | (535) | (536.0) | (569.2) | (648.9) | (381.7) | (330.1) | (424.2) | (371.4) | (328.9) | (248.0) | (147.7) | (56.8) | (32.3) | (16.0) | (6.6) |
| Interest Expense | 62 | 63.0 | 66.0 | 43.0 | 29.4 | 33.3 | 1.1 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0.3 |
| Interest Income | 25 | 36.5 | 26.7 | 11.1 | 1.9 | 7.0 | 13.2 | 9.5 | 4.1 | 3.8 | 2.3 | 0.6 | 0.2 | 0.0 | 0.0 |
| Profitability | |||||||||||||||
| EBITDA | (500) | (469.0) | (516.5) | (640.5) | (410.3) | (139.8) | (389.8) | (177.6) | (312.5) | (244.6) | (146.4) | (56.1) | (34.6) | (16.0) | (6.5) |
| EBIT | (535) | (504.5) | (542.5) | (658.7) | (423.6) | (152.1) | (398.3) | (197.1) | (318.3) | (248.0) | (147.7) | (56.8) | (35.1) | (16.3) | (6.6) |
| Income Before Tax | (571) | (567.6) | (608.5) | (701.7) | (453.0) | (185.4) | (399.4) | (197.1) | (318.3) | (245.8) | (145.6) | (59.8) | (35.1) | (16.3) | (6.8) |
| Income Tax Expense | 4 | 1.6 | (1.8) | 5.7 | 1.0 | 1.2 | 3.3 | 0.5 | (16.2) | 0.0 | 0 | 0 | 0 | 0 | 0 |
| Net Income | (575) | (569.2) | (606.6) | (707.4) | (454.0) | (186.6) | (402.7) | (197.6) | (302.1) | (245.9) | (145.6) | (59.8) | (35.1) | (16.3) | (6.8) |
| Per Share Data | |||||||||||||||
| EPS (Basic) | -5.83 | -6.29 | -8.25 | -10.12 | -6.70 | -3.07 | -7.12 | -3.97 | -7.12 | -6.21 | -3.96 | -2.08 | -1.21 | -0.71 | -0.30 |
| EPS (Diluted) | -5.83 | -6.29 | -8.25 | -10.12 | -6.70 | -3.07 | -7.12 | -3.97 | -7.12 | -6.21 | -3.96 | -2.08 | -1.21 | -0.71 | -0.30 |
| Shares Outstanding | 98.6 | 90.5 | 73.5 | 69.9 | 67.8 | 60.8 | 56.6 | 49.8 | 42.5 | 39.6 | 36.8 | 28.8 | 29.1 | 23.1 | 23.1 |
| Metric | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 | 2018 | 2017 | 2016 |
|---|---|---|---|---|---|---|---|---|---|---|
| Current Assets | ||||||||||
| Cash & Cash Equivalents | 434 | 173.7 | 213.6 | 132.9 | 307.6 | 713.5 | 433.6 | 113.4 | 100.5 | 161.1 |
| Short-Term Investments | 259 | 436.3 | 363.6 | 614.8 | 432.6 | 488.0 | 321.6 | 346.3 | 134.0 | 219.0 |
| Net Receivables | 159 | 121.8 | 73.4 | 40.4 | 28.4 | 23.1 | 32.8 | 12.7 | 5.2 | 0 |
| Inventory | 52 | 45.0 | 34.0 | 26.8 | 16.2 | 13.0 | 11.5 | 7.1 | 0.8 | 0 |
| Other Current Assets | 47 | 40.3 | 47.6 | 68.9 | 0 | 0 | 0 | 0 | 0 | 1.4 |
| Total Current Assets | 951 | 817.1 | 732.2 | 883.9 | 856.6 | 1,295.3 | 851.0 | 522.4 | 244.5 | 498.1 |
| Non-Current Assets | ||||||||||
| Property, Plant & Equipment | 267 | 265.9 | 290.6 | 259.7 | 176.2 | 114.0 | 74.7 | 20.0 | 21.8 | 17.1 |
| Goodwill | 44 | 44.4 | 44.4 | 44.4 | 44.4 | 44.4 | 44.4 | 44.4 | 44.4 | 0 |
| Intangible Assets | 176 | 178.3 | 166.3 | 160.1 | 130.8 | 131.1 | 129 | 129.2 | 141.5 | 0 |
| Long-Term Investments | 59 | 135.0 | 199.9 | 149.0 | 293.9 | 165.9 | 32.9 | 1.8 | 10.0 | 118.0 |
| Other Non-Current Assets | 35 | 62.7 | 57.7 | 48.3 | 20.6 | 8.8 | 3.5 | 3.5 | 3.4 | (92.5) |
| Total Non-Current Assets | 581 | 686.3 | 758.8 | 661.5 | 665.8 | 464.3 | 284.5 | 197.2 | 246.3 | 42.5 |
| Total Assets | 1,532 | 1,503.5 | 1,491.0 | 1,545.4 | 1,522.4 | 1,759.6 | 1,135.5 | 719.6 | 490.8 | 540.6 |
| Current Liabilities | ||||||||||
| Account Payables | 31 | 38.8 | 42.1 | 43.3 | 17.1 | 12.9 | 12.9 | 12.3 | 8.9 | 5.4 |
| Short-Term Debt | 81 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Deferred Revenue | 0 | 0 | 0 | 1.5 | 7.6 | 59.2 | 0 | 0 | 6.0 | 0 |
| Other Current Liabilities | 183 | 87.5 | 142.8 | 0 | 0 | 0 | 0 | 0 | 0 | 37.7 |
| Total Current Liabilities | 384 | 344.2 | 280.4 | 261.2 | 181.4 | 189.6 | 103.3 | 74.7 | 71.0 | 60.3 |
| Non-Current Liabilities | ||||||||||
| Long-Term Debt | 1,171 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Deferred Tax Liabilities | 30 | 30.1 | 0 | 31.7 | 33.3 | 33.3 | 33.3 | 31.2 | 31.2 | 0 |
| Other Non-Current Liabilities | (4) | 836.9 | 904.6 | 880.3 | 352.8 | 335.7 | 315.4 | 4.8 | 5.1 | 6.4 |
| Total Non-Current Liabilities | 1,221 | 897.0 | 935.2 | 931.7 | 418.5 | 415.6 | 378.4 | 35.9 | 36.3 | 6.4 |
| Total Liabilities | 1,605 | 1,241.2 | 1,215.6 | 1,193.0 | 599.8 | 605.2 | 481.7 | 110.7 | 107.3 | 66.7 |
| Stockholders' Equity | ||||||||||
| Common Stock | 0 | 0.1 | 0.1 | 0.1 | 0.1 | 0.1 | 0.1 | 0.1 | 0.0 | 0.0 |
| Retained Earnings | (4,532) | (3,956.8) | (3,387.7) | (2,781.0) | (2,073.6) | (1,619.6) | (1,433.0) | (1,030.3) | (832.7) | (530.5) |
| Accumulated Other Comprehensive Income | 9 | (0.6) | 0.6 | (6.6) | (1.4) | 0.7 | (0.1) | (0.6) | (5.7) | 0.9 |
| Total Stockholders' Equity | (80) | 255.3 | 275.4 | 352.5 | 922.6 | 1,154.4 | 653.8 | 608.9 | 383.5 | 474.0 |
| Total Liabilities & Equity | 1,532 | 1,503.5 | 1,491.0 | 1,545.4 | 1,522.4 | 1,759.6 | 1,135.5 | 719.6 | 490.8 | 540.6 |
| Debt Metrics | ||||||||||
| Total Debt | 1,276 | 40.3 | 43.2 | 31.6 | 42.0 | 48.2 | 37.0 | 0 | 0 | 0 |
| Net Debt | 842 | (133.4) | (170.4) | (101.4) | (265.6) | (665.3) | (396.6) | (113.4) | (100.5) | (161.1) |
| Metric | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 | 2018 | 2017 | 2016 |
|---|---|---|---|---|---|---|---|---|---|---|
| Operating Activities | ||||||||||
| Net Income | (575) | (569.2) | (606.6) | (707.4) | (454.0) | (186.6) | (402.7) | (197.6) | (302.1) | (245.9) |
| Depreciation & Amortization | 35 | 35.5 | 26.0 | 18.2 | 13.2 | 12.3 | 8.5 | 19.5 | 5.8 | 3.4 |
| Stock-Based Compensation | 153 | 158.0 | 135.2 | 130.4 | 105.0 | 85.7 | 82.0 | 80.1 | 68.0 | 48.3 |
| Change in Working Capital | (23) | 13.9 | (15.1) | 60.2 | (63.2) | 104.7 | (15.9) | (24.8) | (20.2) | 26.3 |
| Other Non-Cash Items | (56) | (52.5) | (12.7) | 118.1 | 11.7 | 21.5 | 1.7 | (0.2) | 10.9 | 0.7 |
| Operating Cash Flow | (466) | (414.2) | (474.8) | (380.5) | (338.7) | (132.2) | (345.4) | (290.6) | (253.8) | (161.0) |
| Investing Activities | ||||||||||
| Capital Expenditure | (6) | (7.5) | (46.8) | (146.1) | (73.1) | (43.9) | (24.8) | (4.1) | (2.8) | (10.2) |
| Acquisitions | 0 | 0 | 0 | (75.0) | 0 | 0 | (11.8) | 0 | (142.8) | 0 |
| Purchases of Investments | (186) | (408.6) | (526.4) | (614.7) | (1,012.2) | (850.3) | (707.2) | (509.8) | (230.5) | (442.5) |
| Sales/Maturities of Investments | 444 | 413.3 | 746.2 | 545.1 | 890.9 | 720.6 | 719.0 | 310.2 | 431.6 | 543.8 |
| Other Investing Activities | (16) | (14.9) | (7.5) | (30.8) | (0.9) | (5.6) | 11.8 | 170.3 | 0.9 | (1.2) |
| Investing Cash Flow | 236 | (17.8) | 168 | (291.7) | (195.4) | (179.1) | (13.0) | (33.3) | 56.4 | 89.9 |
| Financing Activities | ||||||||||
| Net Debt Issuance | 392 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | (4.9) | 0 |
| Stock Repurchased | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Dividends Paid | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Other Financing Activities | 0 | 18.3 | 8.4 | 501.2 | 39.6 | 89.1 | 324.1 | 27.8 | 9.3 | 59.2 |
| Financing Cash Flow | 478 | 399.2 | 388.1 | 501.2 | 118.6 | 600.3 | 679.3 | 336.9 | 136.3 | 138.7 |
| Cash Position | ||||||||||
| Net Change in Cash | 253.5 | (35.2) | 81.8 | (172.0) | (416.7) | 290.1 | 320.7 | 12.5 | (60.6) | 67.6 |
| Cash at Beginning | 184.2 | 219.4 | 137.6 | 309.6 | 726.3 | 436.2 | 115.5 | 103.0 | 161.1 | 93.6 |
| Cash at End | 436 | 184.2 | 219.4 | 137.6 | 309.6 | 726.3 | 436.2 | 115.5 | 100.5 | 161.1 |
| Free Cash Flow | (472) | (421.7) | (521.6) | (526.6) | (411.8) | (176.1) | (370.2) | (294.6) | (256.6) | (171.2) |
| Key Metrics | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 | 2018 | 2017 | 2016 | 2015 | 2014 | 2013 | 2012 | 2011 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Income Statement | |||||||||||||||
| Revenue | 673 | 560.2 | 434.2 | 363.3 | 351.4 | 271.0 | 103.7 | 51.5 | 2.6 | 0.1 | 0 | 0 | 0 | 0 | 0 |
| Gross Profit | 564 | 483.5 | 389.0 | 335.0 | 335.4 | 264.9 | 94.7 | 50.3 | 2.6 | (183.1) | (1.4) | 0 | 0 | 0 | 0 |
| Operating Income | (535) | (536.0) | (569.2) | (648.9) | (381.7) | (330.1) | (424.2) | (371.4) | (328.9) | (248.0) | (147.7) | (56.8) | (32.3) | (16.0) | (6.6) |
| Net Income | (575) | (569.2) | (606.6) | (707.4) | (454.0) | (186.6) | (402.7) | (197.6) | (302.1) | (245.9) | (145.6) | (59.8) | (35.1) | (16.3) | (6.8) |
| EPS (Diluted) | -5.83 | -6.29 | -8.25 | -10.12 | -6.70 | -3.07 | -7.12 | -3.97 | -7.12 | -6.21 | -3.96 | -2.08 | -1.21 | -0.71 | -0.30 |
| Balance Sheet | |||||||||||||||
| Cash & Equivalents | 434 | 173.7 | 213.6 | 132.9 | 307.6 | 713.5 | 433.6 | 113.4 | 100.5 | 161.1 | |||||
| Total Assets | 1,532 | 1,503.5 | 1,491.0 | 1,545.4 | 1,522.4 | 1,759.6 | 1,135.5 | 719.6 | 490.8 | 540.6 | |||||
| Total Debt | 1,276 | 40.3 | 43.2 | 31.6 | 42.0 | 48.2 | 37.0 | 0 | 0 | 0 | |||||
| Stockholders' Equity | (80) | 255.3 | 275.4 | 352.5 | 922.6 | 1,154.4 | 653.8 | 608.9 | 383.5 | 474.0 | |||||
| Cash Flow | |||||||||||||||
| Operating Cash Flow | (466) | (414.2) | (474.8) | (380.5) | (338.7) | (132.2) | (345.4) | (290.6) | (253.8) | (161.0) | |||||
| Capital Expenditure | (6) | (7.5) | (46.8) | (146.1) | (73.1) | (43.9) | (24.8) | (4.1) | (2.8) | (10.2) | |||||
| Free Cash Flow | (472) | (421.7) | (521.6) | (526.6) | (411.8) | (176.1) | (370.2) | (294.6) | (256.6) | (171.2) | |||||